Brantley was born with MECP-2 Duplication Syndrome. Many Americans first learned about this progressive, neurological disorder in 2018, when NBC’s Richard Engel first announced this his son had been ...
The FDA has awarded U.S. orphan drug designation and rare pediatric disease designation to Huidagene Therapeutics Co. Ltd.’s HG-204 (AAV-hfCas13Y-gMECP2), an RNA editing therapy based on CRISPR/Cas13Y ...
LAKE CHARLES, La. (KPLC) - At the age of 20, Brody Meaux passed away from MECP2 duplication syndrome - a genetic condition characterized by low muscle tone from infancy, delayed development and ...
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